Dystrophic epidermolysis bullosa approved therapies and global pipeline database.
Duchenne muscular dystrophy oligonucleotide and gene therapy global pipeline database.
Myotonic dystrophy global pipeline database. Full company list, candidates, targets, stage & clinical trials.
Hereditary angioedema approved therapies & global pipeline database.
Limb-girdle muscular dystrophy gene therapy database. Companies, candidates & mechanisms.
Drug development landscape for MCL-1 inhibitors.
Drug development landscape for PRMT5 inhibitors.
Drug development landscape for RAS, SOS1 and SHP2 inhibitors/degraders.
Sickle cell disease approved therapies, global pipeline and Oxbryta sales data.
Spinal muscular atrophy global pipeline and market (net product sales of Spinraza, Evrysdi & Zolgensma).
Targeted protein degradation global pipeline database. Full list of companies, candidates & targets.
Uveal melanoma global pipeline and market (net product sales of KIMMTRAK).
Wet age-related macular degeneration global pipeline and approved therapies.