Dystrophic epidermolysis bullosa approved therapies and global pipeline database.
Duchenne Muscular Dystrophy oligonucleotide and gene therapy global pipeline database.
Myotonic dystrophy global pipeline database. Full company list, candidates, targets, stage, clinical trials and more.
Biotech IPOs in 2023, their targets, platforms, indications and lead-candidate stage.
Biotech IPOs in 2022, their targets, platforms, indications and lead-candidate stage.
Biotech IPOs in 2021, their targets, platforms, indications and lead-candidate stage.
Limb-girdle muscular dystrophy gene therapy database. Companies, candidates, mechanisms, and more.
Drug development landscape in targeting MCL-1.
Drug development landscape in targeting PRMT5.
Drug development landscape in targeting RAS, SOS1 and SHP2 within the mitogenic pathway.
Sickle cell disease approved therapies, global pipeline and Oxbryta sales data.
Spinal muscular atrophy global pipeline and market (quarterly net product sales of Spinraza, Evrysdi & Zolgensma).
Targeted protein degradation global pipeline database. Full list of companies developing TPD, lead candidates, targets, stage of development.
Uveal melanoma global pipeline and market (net product sales of KIMMTRAK).
Wet age-related macular degeneration global pipeline and approved therapies.